Risdiplam, the First Approved Small Molecule Splicing Modifier Drug as a Blueprint for Future Transformative Medicines
Hasane Ratni*, Renata S. Scalco, and Alexander H. Stephan*
ACS Med. Chem. Lett. 2021, 12, 6, 874–877
- DOI:
http://dx.doi.org/10.1021/acsmedchemlett.0c00659